Volume 12 (2024)
Volume 11 (2023)
Volume 10 (2022)
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Volume 1 (2013)
Keywords = Enzyme replacement therapy
Number of Articles: 2
The Effects of Enzyme Replacement Therapy in Patients with Mucopolysaccharidosis Type 1: A Case Series Study
Volume 10, Issue 4 , April 2022, , Pages 15853-15864
Abstract
Background: Mucopolysaccharidosis type I (MPS1) is caused by mutations in the gene which encodes the enzyme alpha-L-iduronidase. Deficiency of this enzyme causes a range of clinical ... Read MoreMedication Cost of Enzyme Replacement Therapy for Mucopolysaccharidoses in Iran
Volume 9, Issue 12 , December 2021, , Pages 14988-14996